In vivo gene editing: CRISPR therapy for hereditary angioedema https://ymaho.com/in-vivo-gene-editing-crispr-therapy-for-hereditary-angioedema
Single-dose CRISPR therapy NTLA-2002 reduced hereditary angioedema attacks by 87% in phase III. Learn how this will change treatment and pave the way to a cure.
In vivo gene editing: phase 3 of HAE therapy successful https://ymaho.com/in-vivo-gene-editing-phase-3-of-hae-therapy-successful
First ever successful phase 3 in vivo gene editing: lonvo-z therapy reduces HAE attacks by 87%. Learn about the breakthrough and discontinuation of prophylaxis.
CRISPR in vivo reduces cholesterol by 60% in VERVE-102 study https://ymaho.com/crispr-in-vivo-reduces-cholesterol-by-60-in-verve-102-study
Single infusion of VERVE-201 sustainably lowers LDL by more than 60%. Learn how CRISPR editing is changing the hypercholesterolemia therapy market. Read the analysis.
CRISPR therapy in vivo: Intellia study 87% efficacy in HAE https://ymaho.com/crispr-therapy-in-vivo-intellia-study-87-efficacy-in-hae
Phase 3 HAELO: single CRISPR infusion reduced hereditary angioedema attacks by 87% vs placebo. First in vivo therapy on the verge of registration. Details, insights, forecasts.
Personalized CRISPR therapy saved an infant: in vivo breakthrough https://ymaho.com/personalized-crispr-therapy-saved-an-infant-in-vivo-breakthrough
A child with the ultra-rare CPS1 mutation survived thanks to personalized CRISPR therapy in 6 months. Learn about the breakthrough in genetic engineering and N-of-1 platforms.
Intellia CRISPR therapy: FDA filing for lonvo-z for HAE https://ymaho.com/intellia-crispr-therapy-fda-filing-for-lonvo-z-for-hae
Intellia has filed the world's first application for an in vivo CRISPR therapy, lonvo-z, for hereditary angioedema (HAE). 87% reduction in attacks, 62% attack-free. Risk, market, and forecast analysis. Read.
AI mini-proteins control GPCR receptors: a breakthrough in pharma https://ymaho.com/ai-mini-proteins-control-gpcr-receptors-a-breakthrough-in-pharma
AI created mini-proteins for precise activation of GPCR in vivo. Superior to antibodies, fewer side effects. Market and impact analysis. Read more.
Intellia CRISPR therapy: phase 3 data on edema — breakthrough https://ymaho.com/intellia-crispr-therapy-phase-3-data-on-edema-breakthrough
Intellia presented long-awaited phase III data of CRISPR therapy lonvo-z for hereditary angioedema: 87% reduction in attacks, 62% of patients attack-free. Learn about the breakthrough in in vivo genome editing.